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Rare Diseases Stocks List

Symbol Name Country Exchange
LPCUF Lees Pharmaceutical Holdings Ltd US OTC
CSCI COSCIENS Biopharma Inc. US US
EIGRQ Eiger BioPharmaceuticals Inc US US
MDMXF medmix AG US US
RICFY Recordati Industria Chimica e Farmaceutica S.p.A. US US
08D MIRUM PHARMAC. DL-0001 DE F
12X1 Anavex Life Sciences Corp DE F
1GDA KEMPHARM INC. DL-0001 DE F
1KPA PROTARA THERAPEUT.DL-001 DE F
30S SANIONA AB (PUBL) DE F
48Q X4 PHARMACEUTIC. DL-001 DE F
4KB Krystal Biotech Inc DE F
61Y MARINUS PHARMAC. DL-001 DE F
9EN PHARVARIS N.V. EO -12 DE F
AB3A Sarepta Therapeutics Inc DE F
AM6 Amicus Therapeutics Inc DE F
BH3 PTC Therapeutics Inc. DE F
BM8 BioMarin Pharmaceutical Inc DE F
BO1 BioCryst Pharmaceuticals Inc DE F
DR6 ACADIA Pharmaceuticals Inc DE F